Medical News

One of the most prominent challenges facing patients of any rare disease is access to and ... read more
The impact of changes in policy, programs, and attitudes towards rare diseases was on full display ... read more
While the rare disease community is aware of the recent efforts from the US Food and ... read more
While focusing on rare diseases sets the 2019 National Organization for Rare Diseases (NORD) and Orphan ... read more
A new study from the 2019 National Organization for Rare Diseases (NORD) and Orphan Products Breakthrough ... read more
Data presented at the 2019 National Organization for Rare Diseases (NORD) and Orphan Products Breakthrough Summit ... read more
With rare diseases impacting small patient populations and often manifesting in unique ways with every patient, ... read more
By definition, patients with a rare disease are always part of a small group and, because ... read more